Ausgabe 8/2025
Inhalt (39 Artikel)
Infectious complications in CLL/SLL patients receiving Bruton's Tyrosine Kinase inhibitors – systematic review and meta-analysis of randomized controlled trials
- Open Access
- Review
Shira Buchrits, Gal Trieman, Odil Giladi, Liron Hofstetter, Ronit Gurion, Galit Granot, Adi Shacham-Abulafia, Pia Raanani, Anat Gafter-Gvili
The evaluation, management, and future of indolent systemic mastocytosis
- Open Access
- Review
Arjun Syal, Jennifer Toh, Alissa McInerney, Douglas Tremblay
Next-generation Bruton tyrosine kinase inhibitors and degraders in the treatment of B-cell malignancies: advances and challenges
- Open Access
- Review
Yao Wang, Yaping Zhang, Jiaqi Liu, Yongning Jiang, Jianyong Li, Wenyu Shi
Prognostic significance of in patients with chronic lymphocytic leukemia: A meta-analysis
- Open Access
- Review
Liping Huang, Xinyi Shi, Ningning Tang, Juan Liu, Yanli Liang, Xin Wang
Beyond transfusions and transplants: genomic innovations rewriting the narrative of thalassemia
- Open Access
- Review
Liangbin Shi, Xili Yan, Yanwei Xia, Yingdi Zhao, Xiuling Zhu, Qiang Li, Zhiliang Xu
Somatic mutations and the efficacy of immunosuppressive therapy in severe/very severe aplastic anemia and transfusion-dependent nonsevere aplastic anemia
- Open Access
- Research
Lei Ye, Li Zhang, Donglei Zhang, Xin Zhao, Yuan Li, Youzhen Xiong, Liwei Fang, Meili Ge, Jun Shi, Fengkui Zhang, Liping Jing
Optimizing hemophagocytic lymphohistiocytosis screening in children: validation of the HLH-Screen score
- Open Access
- Research
Xiao Li, Zhexuan Tang, Lifang Zhou, Xun Li, Lihui Deng, Haipeng Yan, Xiangyu Wang, Longlong Xie, Ting Luo, Yufan Yang, Xinping Zhang, Jiaotian Huang, Yefei Lei, Zhenghui Xiao, Xiulan Lu
Predictive factors of romiplostim response in patients with refractory aplastic anemia: data from two clinical trials
- Open Access
- Research
Jun Ho Jang, Kinuko Mitani, Yoshiaki Tomiyama, Koji Miyazaki, Koji Nagafuji, Kensuke Usuki, Nobuhiko Uoshima, Tomoaki Fujisaki, Hiroshi Kosugi, Itaru Matsumura, Ko Sasaki, Masahiro Kizaki, Masashi Sawa, Michihiro Hidaka, Naoki Kobayashi, Satoshi Ichikawa, Yuji Yonemura, Kenta Murotani, Mami Shimizu, Akira Matsuda, Keiya Ozawa, Shinji Nakao, Jong Wook Lee
Analysis of fecal microbiome in Chinese patients with non-severe aplastic anemia
- Open Access
- Research
Xiaolan Zhang, Jingjing Xie, Heng Wang, Jun Li
Genetic modifiers of frequent vaso-occlusive hospitalizations among individuals with sickle cell disease (SCD)
- Open Access
- Research
Mina Cintho Ozahata, Isabel Gomes, Beatriz A. Oliveira, Miriam Park, Daniela O. W. Rodrigues, Anna Bárbara Carneiro-Proietti, Cláudia Máximo, Allison Ashley-Koch, Marilyn Telen, Shannon Kelly, Brian Custer, Ester Cerdeira Sabino, Carla Luana Dinardo
Analysis of the current situation and influencing factors of home treatment for children with hemophilia in China
- Open Access
- Research
Chunli Wang, Runhui Wu, Xumei Wang, Wei Chi, Xinyi Wu, Guoqing Liu
Three novel heterozygous ANK1 loss-of-function variants cause hereditary spherocytosis in Chinese families
- Open Access
- Research
Yang Wang, Tao Liu, Wen Wang, Yuzhuopu Li, Li Xiao, Yan Xiang, Lan Huang, Yongjie Zhang, Jie Yu
Urinary metabolomics predicts early rituximab response in steroid-nonresponsive pediatric patients with primary immune thrombocytopenia
- Open Access
- Research
Yuncui Yu, Zhenping Chen, Jing Wei, Xingjuan Xie, Juntao Ouyang, Zheyan Lin, Jingyao Ma, Peng Guo, Runhui Wu, Jingang Gui
Semen quality in acute leukemia patients: a retrospective study
- Open Access
- Research
Alessandra Buonacquisto, Maria Ilaria Del Principe, Francesco Pallotti, Serena Bianchini, Elisa Buzzatti, Luisa Caponecchia, Sabina Chiaretti, Gaia Cicolani, Anna Chiara Conflitti, Silvia Di Chiano, Ludovica Fucci, Deborah Kasmi, Clara Minotti, Giovangiacinto Paterno, Ilaria Tiravanti, Adriano Venditti, Francesco Lombardo, Donatella Paoli
t(8;21)AML patients with RUNX1e6::RUNX1T19a splice variant have poor prognosis
- Open Access
- Research
Yuying Fan, Lanhui Chen, Sijin Liu, Jinwen Dang, Jianmei Chang, Caifeng Guo, Yang Xu, Wenzheng Guo, Hongwei Wang, Yanhong Tan
Clinical characteristics and outcome of pediatric patients with high-risk acute promyelocytic leukemia, with special focus on risk factors of early death
- Open Access
- Research
Qinli Gao, Yiqiao Chen, Shaohua Le, Nainong Li, Cai Chen
Sirolimus modulates the erythroid differentiation of K562 cells by upregulating SHP1
- Open Access
- Research
Yuan Yang, Zengwei Tang, Qinglin Hu, Chen Yang, Miao Chen, Hongmei Jing, Bing Han
Gene expression analysis of patients with chronic myeloid leukemia who discontinued tyrosine kinase inhibitor
- Open Access
- Research
Hyunkyung Park, Hyeong-Joon Kim, Sang-Kyun Sohn, Yoonsuk Baik, Dongho Kim, Sung-Yeoun Lee, Jee Hyun Kong, Hawk Kim, Dong-Yeop Shin, Jae-Sook Ahn, Jinny Park, Seonyang Park, Inho Kim
Durable outcomes with manageable safety leading to prolonged survival with tagraxofusp for treatment-naïve patients with blastic plasmacytoid dendritic cell neoplasm: real world results from a European Named Patient Program
- Open Access
- Research
Marco Herling, Emanuele Angelucci, Tobias Matthieu Benoit, Giulia Rivoli, Antonio Curti, Katharina S. Götze, Stefan Wirths, Dimoula Erakli, Michael Zuurman, Eric Deconinck
The prognostic value of hemoglobin, albumin, lymphocyte, and platelet (HALP) score in low-risk and early-stage extranodal natural killer/T cell lymphoma
- Open Access
- Research
Na Li, Jing Huang, Yuping Xie, You Feng, Shihui Min, Li-qun Zou
De-escalated Teclistamab dosing in relapsed/refractory multiple myeloma: Czech myeloma group real-world evidence analysis
- Open Access
- Research
Martin Stork, Jakub Radocha, Jana Mihalyova, Ivan Spicka, Tomas Pika, Alexandra Jungova, Ivanna Boichuk, Klara Mensikova, Jan Straub, Frantisek Sedlak, Jiri Minarik, Petra Krhovska, Denisa Novakova, Michaela Hornakova, Zdenka Knechtova, Nela Sendlerova, Tereza Dekojova, Vladimir Maisnar, Tomas Jelinek, Roman Hajek, Ludek Pour
Prophylactic Tocilizumab prior to infusion of CD19 CAR T-cells reduces therapy-related complications in older lymphoma patients
- Open Access
- Research
Sebastian M. Stolz, Albulena Musa, Adrian Bachofner, Andriyana K. Bankova, Elise Gourri, Markus G. Manz, Max J. Rieger, Dominik Schneidawind, Nathan Wolfensberger, Thorsten Zenz, Wiebke Rösler
Exploring the baseline cardiac function and its correlation with risk stratification in children diagnosed with acute lymphoblastic leukemia
- Open Access
- Research
Diana R. Lazar, Dana Maniu, Florin-Leontin Lazar, Cristina Blag, Madalina Bota, Mihnea Zdrenghea, Simona Cainap
Pola-R-CHP performed well in first-line Polarix trial-ineligible and IPI 0–1 DLBCL patients
- Open Access
- Research
Yuhong Ren, Luya Cheng, Jingli Zhuang, Zhimei Wang, Ling Yuan, Zhixiang Cheng, Yang Ke, Weiguang Wang, Jing Li, Peng Liu
Real-world efficacy and safety outcomes of acalabrutinib in chronic lymphocytic leukemia: primary results of a French multicentre observational study (NAOS)
- Open Access
- Research
Anne Quinquenel, Stéphane Leprêtre, Marie Sarah Dilhuydy, Lucile Bussot, Zora Marjanovic, Omar Benbrahim, Romain Guièze, Alberto Santagostino, Caroline Dartigeas, Pierre Feugier, Damien Roos-Weil, Ghandi Damaj, Kamel Laribi, Loic Ysebaert, Vincent Levy
Autologous stem cell transplantation from 2011 to 2022 in Japanese patients aged ≥ 65 years with relapsed or refractory diffuse large B-cell lymphoma
- Open Access
- Research
Satoshi Yamasaki, Shohei Mizuno, Kota Yoshifuji, Eri Matsuki, Masashi Sawa, Takashi Akasaka, Naoyuki Uchida, Hitoji Uchiyama, Keisuke Kataoka, Nobuhiro Hiramoto, Yoshinobu Kanda, Kazuya Ishiwata, Toshio Wakayama, Takahiro Fukuda, Makoto Yoshimitsu, Makoto Onizuka, Marie Ohbiki, Yoshiko Atsuta, Ritsuro Suzuki, Shinichi Kako
Comparative longitudinal analysis of pulmonary function post-pediatric Allo-HSCT: benign vs. malignant diseases and early predictors
- Open Access
- Research
Hongjuan Li, Yan Gu, Xiaowei Zhao, Guoyu Ding, Yuqi Zhao, Xiaoyue Zhang, Yan Han, Xue Li, Hongmei Wang
Second allogeneic transplantation in relapsed acute leukemia – a risk worth taking?
- Open Access
- Research
Patrycja Zielińska, Karolina Gruenpeter, Agata Wieczorkiewicz-Kabut, Krzysztof Białas, Anna Koclęga, Izabela Noster, Izabela Szewczyk, Kinga Boral, Katarzyna Wiśniewska-Piąty, Aleksandra Butrym, Jarosław Czyż, Ewa Lutwin, Grzegorz Helbig
Effectiveness of venetoclax based therapy in t(11;14) multiple myeloma with extensive extramedullary disease: a case report
- Open Access
- Case Report
Kerstin Brinkert, Bernd Heinrich, Annamaria Brioli, Michael Heuser, Hans Heinrich Kreipe, Florian H. Heidel, Arnold Ganser, Gernot Beutel
Sickle cell β-thalassemia diagnosed at age 40: a case report
- Open Access
- Case Report
Christos G. Nikolaidis, Despoina Gyriki, Dimitrios G. Gogos, Elisavet Stavropoulou
Successful treatment with mesenchymal stromal cells-Frankfurt am Main in a pediatric patient with steroid-refractory and ruxolitinib-refractory acute gastrointestinal graft-versus-host disease
- Open Access
- Case Report
Jana Ernst, Steffen Reinsch, Hans-Joachim Mentzel, Till Milde, Bernd Gruhn
Hyperhemolysis in a sickle cell disease patient in pregnancy
- Open Access
- Case Report
Kristen Warncke, Alecia Nero, Ravindra Sarode, Brian D. Adkins, Jamie Morgan, Natalie Bavli
Clinical features and fusion gene analysis of two Torque Teno Mini virus associated acute promyelocytic leukemia cases
- Open Access
- Case Report
Deyan Liu, Jiaqi Chen, Yu Luo, Shu Yan, Hua Nan, Xue Chen, Zhongyuan Lin, Liejun Jiang, Huihe Tang, Hongyan Ma, Yumeng Niu, Jiancheng Fang, Panxiang Cao, Lili Yuan, Xiaoli Ma, Xiaosu Zhou, Fanyong LV, Yan Dai, Hongxing Liu
Biphenotypic NK-Large granular lymphocytic leukemia with aggressive clinical features: a case report and literature review
- Open Access
- Case Report
Beichen Liu, Tengteng Yu, Na Zhou, Shuhua Yi
Consequences and impacts of PEG-IFNα2a shortage: first lessons from a MPN French center
- Open Access
- Brief Report
Laura Cailly, Wayne-Corentin Lambert, Jean-Richard Eveillard, Brigitte Pan-Petesch, Laura Herbreteau, Laetitia Rio, Lanig Civi, Adrian Tempescul, Florence Dalbies, Hussam Saad, Cristina Bagacean, Marie-Anne Couturier, Gaelle Guillerm, Eric Lippert, Jean-Christophe Ianotto
Venetoclax plus azacitidine as genetic-driven bridge-to-transplant therapy for IDH2-mutated acute myeloid leukaemia (AML) refractory to intensive chemotherapy: proof-of-concept case reports
- Open Access
- Correspondence
Gaetano Cimino, Matteo Caridi, Valeria Cardinali, Sofia Sciabolacci, Sara De Santis, Camilla Rellini, Caterina Matteucci, Cristina Mecucci, Paolo Sportoletti, Francesco Zorutti, Alessandra Carotti, Roberta La Starza, Antonio Pierini, Maria Paola Martelli
Validation of the simplified geriatric prognostic index in a Hellenic database of older patients (≥ 70 years old) with diffuse large B-cell lymphoma and similar disorders
- Open Access
- Correspondence
Theodoros P. Vassilakopoulos, Fotios Panitsas, Maria Panagiota Arapaki, Amalia Anastasopoulou, Christina Apostolopoulou, Evgenia Verrou, Christina H. Kalpadakis, Alexia Piperidou, Athanasios Liaskas, Sotirios Sachanas, Theodora Triantafyllou, Aikaterini Bitsani, Maria Dimou, Maria Anastasia Ioakeim, Panagiotis Tsirigotis, Marina P. Siakantaris, Vassiliki Pappa, Panayiotis Panayiotidis, Gerassimos A. Pangalis, Eirini Katodritou, Maria K. Angelopoulou, Sotirios G. Papageorgiou
The incidence of paroxysmal nocturnal hemoglobinuria cell clones in the Nordic countries
- Open Access
- Correspondence
Torkild Høieggen Pedersen, Eirik Tjønnfjord, Eva-Stina Korkama, Mariann Vikman, Ahmad Ahmadi, Ulrik Malthe Overgaard, Christian Kjellander
Correction to: Mutational heterogeneities in STAT3 and clonal hematopoiesis-related genes in acquired pure red cell aplasia
- Open Access
- Correction
Toru Kawakami, Fumihiro Kawakami, Shuji Matsuzawa, Taku Yamane, Yuga Mizuno, Ami Asakura, Daigo Higano, Shotaro Miyairi, Kaoko Sakai, Sayaka Nishina, Hitoshi Sakai, Yasushi Kubota, Yumiko Higuchi, Hideyuki Nakazawa, Fumihiro Ishida