Molecular Therapy - Nucleic Acids
Volume 12, 7 September 2018, Pages 730-740
Original ArticleSplice-Modulating Oligonucleotide QR-110 Restores CEP290 mRNA and Function in Human c.2991+1655A>G LCA10 Models
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open access
Graphical Abstract
Keywords
retinal dystrophy
oligonucleotide
stem cell
organoid
therapy
QR-110
Cited by (0)
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These authors contributed equally to this work.
© 2018 The Author(s).