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Advances in Therapy

Ausgabe 4/2023

Inhalt (39 Artikel)

Open Access Review

TMPRSS6 as a Therapeutic Target for Disorders of Erythropoiesis and Iron Homeostasis

Tomas Ganz, Elizabeta Nemeth, Stefano Rivella, Paul Goldberg, Andrew R. Dibble, Michael L. McCaleb, Shuling Guo, Brett P. Monia, Terrance D. Barrett

COVID-19 Review

What Do We Need to Know About Rising Rates of Idiopathic Pulmonary Fibrosis? A Narrative Review and Update

Joseph V. Pergolizzi Jr., Jo Ann LeQuang, Marco Varrassi, Frank Breve, Peter Magnusson, Giustino Varrassi

Review

Aminoglycoside-Related Nephrotoxicity and Ototoxicity in Clinical Practice: A Review of Pathophysiological Mechanism and Treatment Options

Tyler A. Le, Tasneem Hiba, Disha Chaudhari, Arielle N. Preston, Zachary R. Palowsky, Shahab Ahmadzadeh, Sahar Shekoohi, Elyse M. Cornett, Alan D. Kaye

Review

Tetracycline-, Doxycycline-, Minocycline-Induced Pseudotumor Cerebri and Esophageal Perforation

Alexis L. Angelette, Lauren L. Rando, Reena D. Wadhwa, Ashley A. Barras, Blake M. Delacroix, Norris C. Talbot, Shahab Ahmadzadeh, Sahar Shekoohi, Elyse M. Cornett, Adam M. Kaye, Alan D. Kaye

Open Access Review

Histology-Agnostic Drugs: A Paradigm Shift—A Narrative Review

André Mansinho, Ricardo Miguel Fernandes, António Vaz Carneiro

Open Access Review

Breast Cancer Screening Should Embrace Precision Medicine: Evidence by Reviewing Economic Evaluations in China

Jingjing Jiang, Shan Jiang, Antonio Ahumada-Canale, Zhuo Chen, Lei Si, Yawen Jiang, Li Yang, Yuanyuan Gu

Open Access Review

GLP-1 RAs in Spain: A Short Narrative Review of Their Use in Real Clinical Practice

Irene Romera, Miriam Rubio-de Santos, Sara Artola, Carmen Suárez Fernández, Ignacio Conget

Open Access Original Research

The Impact of Obesity in Saudi Arabia: Healthcare Resource Use and Costs Associated with Obesity-Related Complications

Hussain A. Al-Omar, Ali Alshehri, Abdulmohsen Abanumay, Hana Alabdulkarim, Ali Alrumaih, Mahmoud S. Eldin, Saleh A. Alqahtani

Original Research

Comparison of Outcomes of Phacoemulsification Combined with Endoscopic Cyclophotocoagulation, iStent, or Both in the Management of Open-Angle Glaucoma

Galia A. Deitz, Jennifer L. Patnaik, Cara E. Capitena Young, Monica K. Ertel, Jeffrey R. SooHoo, Leonard K. Seibold, Malik Y. Kahook, Mina B. Pantcheva

Original Research

Bioinformatics Identification of Therapeutic Gene Targets for Gastric Cancer

Yuanting Li, Minghao Chen, Qing Chen, Min Yuan, Xi Zeng, Yan Zeng, Meibo He, Baiqiang Wang, Bin Han

Open Access Original Research

Real-World Safety and Tolerability of Nintedanib in Patients with Idiopathic Pulmonary Fibrosis: Interim Report of a Post-Marketing Surveillance in Japan

Takashi Ogura, Yoshikazu Inoue, Arata Azuma, Sakae Homma, Yasuhiro Kondoh, Katsumi Tanaka, Kaori Ochiai, Yukihiko Sugiyama, Toshihiro Nukiwa

Original Research

Human Albumin Infusion for the Management of Liver Cirrhosis and Its Complications: An Overview of Major Findings from Meta-analyses

Xiaojie Zheng, Zhaohui Bai, Ting Wang, Fernando G. Romeiro, Andrea Mancuso, Cyriac A. Philips, Yu J. Wong, Filipe G. Nery, Xingshun Qi

Open Access Original Research

Self-Administration of Burosumab in Children and Adults with X-Linked Hypophosphataemia in Two Open-Label, Single-Arm Clinical Studies

Takuo Kubota, Noriyuki Namba, Hiroyuki Tanaka, Koji Muroya, Yasuo Imanishi, Yasuhiro Takeuchi, Masanori Kanematsu, Wei Sun, Yoshiki Seino, Keiichi Ozono

Open Access Original Research

Safety of Roxadustat Versus Erythropoiesis-Stimulating Agents in Patients with Anemia of Non-dialysis-Dependent or Incident-to-Dialysis Chronic Kidney Disease: Pooled Analysis of Four Phase 3 Studies

Jonathan Barratt, Frank Dellanna, Jose Portoles, Gabriel Choukroun, Luca De Nicola, James Young, Nada Dimković, Michael Reusch

Original Research

Remote-Access Thyroidectomy in the Pediatric Population: a Systematic Review

Oded Cohen, Antti A. Mäkitie, Avi Khafif, Ashok R. Shaha, Gregory Randolph, Andrés Coca-Pelaz, Alfio Ferlito

Open Access Original Research

Comparative Effectiveness of Pegcetacoplan Versus Ravulizumab and Eculizumab in Complement Inhibitor-Naïve Patients with Paroxysmal Nocturnal Hemoglobinuria: A Matching-Adjusted Indirect Comparison

Raymond Wong, Jesse Fishman, Koo Wilson, Michael Yeh, Mohammed Al-Adhami, Abigail Zion, Christopher W. Yee, Lynn Huynh, Mei Sheng Duh

Original Research

Genetic Evidence Supporting Causal Roles of mTOR-Dependent Proteins in Rheumatic Fever: A Two-Sample Randomized Mendelian Study

Yan-Fei Mu, Qian Wang, Jing-Xi Hu, Qi Wang, Yao-Chen Zhang, Ke-Yi Fan, Zi-Yi Han, He-Yi Zhang, Ting Cheng, Rong Zhao, Shan Song, Jun Qiao, Sheng-Xiao Zhang, Cai-Hong Wang

Open Access Original Research

High Clinical Burden of Influenza Disease in Adults Aged ≥ 65 Years: Can We Do Better? A Systematic Literature Review

Jakob Langer, Verna L. Welch, Mary M. Moran, Alejandro Cane, Santiago M. C. Lopez, Amit Srivastava, Ashley L. Enstone, Amy Sears, Kristen J. Markus, Maria Heuser, Rachel M. Kewley, Isabelle J. Whittle

Open Access Original Research

Safety, Tolerability and Pharmacokinetics of Single and Multiple Doses of Mirogabalin in Healthy Chinese Participants: A Randomized, Double-Blind, Placebo-Controlled Study

Yi Li, Kaoru Toyama, Takafumi Nakatsu, Hitoshi Ishizuka, Hailan Wu, Guoying Cao, Jicheng Yu, Yu Wang, Xiaofen Liu, Beining Guo, Jufang Wu, Peimin Yu, Zhen Hong, Jing Zhang, Xiaojie Wu

Open Access Original Research

Levothyroxine Bioequivalence Study and Its Narrow Therapeutic Index: Comparative Bioavailability Results Between Two Formulations Available in Latin America

Carlos Walter Bertoncini, Maria Juliana Cruz Palacios, María Carolina Fritz, Maria Pía Rodriguez, Cecilia Acevedo, Gabriel Alejandro Hunzicker, Mario César Dominguez, Isaac Arbeláez

Open Access Original Research

Economic Impact of Transformation to Acute Myeloid Leukemia Among Actively Managed Patients with Higher-Risk Myelodysplastic Syndromes in the United States

Vamsi Kota, Augustina Ogbonnaya, Eileen Farrelly, Bridgette Kanz Schroader, Aditya Raju, Fjoralba Kristo, Mehul Dalal

Open Access Original Research

Patient and Healthcare Professional Insights of Home- and Remote-Based Clinical Assessment: A Qualitative Study from Spain and Brazil to Determine Implications for Clinical Trials and Current Practice

Simón Lalanza, Catalina Peña, Carlos Bezos, Nancy Yamauchi, Viviane Taffner, Kelly Rodrigues, Marta Garcia Manrique, Ana Rubio Jareño, Andreia Lemos Gil

Open Access Original Research

Effectiveness and Safety of Apixaban vs Warfarin in Patients with Venous Thromboembolism with Risk Factors for Bleeding or for Recurrences

Alexander T. Cohen, Janvi Sah, Amol D. Dhamane, Dionne M. Hines, Theodore Lee, Lisa Rosenblatt, Birol Emir, Allison Keshishian, Huseyin Yuce, Xuemei Luo

Original Research

Association Between Multidrug-Resistant Bacteria and Mortality in Critically Ill Patients

Gary Duclos, Ines Lakbar, Mohamed Boucekine, Georges Lolo, Nadim Cassir, Marc Leone

Open Access Original Research

Venous Thromboembolism Recurrence Among Patients Who Abandon Oral Anticoagulant Therapy in the USA: A Retrospective Longitudinal Study

Mark Alberts, Maryia Zhdanava, Dominic Pilon, Gabrielle Caron-Lapointe, Patrick Lefebvre, Brahim Bookhart, Akshay Kharat

Open Access Original Research

Adherence to Triple Single-Pill Combination of Perindopril/Indapamide/Amlodipine: Findings from Real-World Analysis in Italy

Claudio Borghi, Pathiyil Balagopalan Jayagopal, Alexandra Konradi, Luiz Aparecido Bortolotto, Luca Degli Esposti, Valentina Perrone, Jacques R. Snyman

Open Access Original Research

Development and Preliminary Validation of an Instrument to Measure Symptoms and Impacts in Patients with Proliferative Diabetic Retinopathy

Diana Rofail, Steven Sherman, Christopher Hartford, Adele Levine, Jessica Baldasaro, Patrick Marquis, Rohini Rao, Diana V. Do

Open Access Original Research

Apremilast Use in Severe Psoriasis: Real-World Data from Central and Eastern Europe

Petra Cetkovská, Iva Dediol, Marija Šola, Martina Kojanová, Katarina Trčko, Antoanela Čarija, Romana Čeović, Daniela Ledić-Drvar, Marija Kaštelan, Andina Hrabar, Myriam Cordey Missoup, Khalid Mamun

Open Access Original Research

Cost Analysis of Aprotinin Reintroduction in French Cardiac Surgery Centres: A Real-World Data-Based Analysis

Pascal Colson, Jean-Luc Fellahi, Philippe Gaudard, Sophie Provenchère, Bertrand Rozec

Open Access Original Research

Association Between Myasthenia Gravis–Activities of Daily Living (MG-ADL) and EQ-5D-5L Utility Values: The Additional Effect of Efgartigimod on Utilities

Sarah Dewilde, Cynthia Z. Qi, Glenn Phillips, Sergio Iannazzo, Mathieu F. Janssen

Original Research

Patient Blood Management in Transurethral Resection Surgery: Overview and Strategy Analysis from a French Tertiary Hospital

Bruno Pastene, Raphaël Bernard, Manon Colin, Claire Zunino, Lénaïck Chabert-Vaudran, Cyrille Bastide, Laurent Zieleskiewicz, Marc Leone

Open Access Original Research

Real-World Racial Variation in Treatment and Outcomes Among Patients with Peripheral Artery Disease

Keith C. Ferdinand, Kay Sadik, Richard Browne, Urvi Desai, Patrick Lefebvre, Dominique Lejeune, Malena Mahendran, François Laliberté, Lisa Matay, David G. Armstrong

Open Access Brief Report

Baricitinib Safety for Events of Special Interest in Populations at Risk: Analysis from Randomised Trial Data Across Rheumatologic and Dermatologic Indications

Peter C. Taylor, Thomas Bieber, Rieke Alten, Torsten Witte, James Galloway, Walter Deberdt, Maher Issa, Ewa Haladyj, Inmaculada De La Torre, Susanne Grond, Andreas Wollenberg

Open Access Brief Report

Safety and Effectiveness Analyses of Dolutegravir/Lamivudine in Patients with HIV: 2-Year Report of Post-Marketing Surveillance in Japan

Ayano Tofukuji, Haruyuki Hongo, Takako Nagao, Akemi Sebata, Miwako Suzuki, Yuko Maeno, Eiji Kurosaki, Akiko Fukuda, Tomoyuki Watanabe

Study Protocol

Clinical Characteristics, Treatment Patterns, and Effectiveness in Chinese Patients with Angina Pectoris Using Electronic Patient-Reported Outcomes: Protocol for a Multicenter, Prospective, Cohort Study (GREAT)

Xiliang Zhao, Zichuan Tong, Liling Sun, Qihua Zhang, Xin Du, Su’e Xu, Chengning Shen, Ying Wei, Wei Liu, Lifu Miao, Yong Zeng

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Herzinfarkt mit 85 – trotzdem noch intensive Lipidsenkung?

16.05.2024 Hypercholesterinämie Nachrichten

Profitieren nach einem akuten Myokardinfarkt auch Betroffene über 80 Jahre noch von einer intensiven Lipidsenkung zur Sekundärprävention? Um diese Frage zu beantworten, wurden jetzt Registerdaten aus Frankreich ausgewertet.

Erstmanifestation eines Diabetes-Typ-1 bei Kindern: Ein Notfall!

16.05.2024 DDG-Jahrestagung 2024 Kongressbericht

Manifestiert sich ein Typ-1-Diabetes bei Kindern, ist das ein Notfall – ebenso wie eine diabetische Ketoazidose. Die Grundsäulen der Therapie bestehen aus Rehydratation, Insulin und Kaliumgabe. Insulin ist das Medikament der Wahl zur Behandlung der Ketoazidose.

CKD bei Diabetes: Neuheiten und Zukunftsaussichten

16.05.2024 DDG-Jahrestagung 2024 Kongressbericht

Jeder Mensch mit Diabetes muss auf eine chronische Nierenerkrankung gescreent werden – diese neue Empfehlung spricht die KDIGO aus. Die Therapie erfolgt individuell und je nach Szenario mit verschiedenen Substanzklassen. Künftig kommt wahrscheinlich, neben RAS-Hemmung, SGLT2-Inhibition und nsMRA, eine vierte Therapiesäule hinzu.

Riesenzellarteriitis: 15% der Patienten sind von okkulter Form betroffen

16.05.2024 Riesenzellarteriitis Nachrichten

In einer retrospektiven Untersuchung haben Forschende aus Belgien und den Niederlanden die okkulte Form der Riesenzellarteriitis genauer unter die Lupe genommen. In puncto Therapie und Rezidivraten stellten sie keinen sehr großen Unterschied zu Erkrankten mit kranialen Symptomen fest.

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