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Advances in Therapy

Ausgabe 4/2024

Inhalt (34 Artikel)

Open Access Commentary

Managing Gastrointestinal Symptoms Resulting from Treatment with Trofinetide for Rett Syndrome: Caregiver and Nurse Perspectives

Rebecca Moore, Joshua Poulsen, Lindsay Reardon, Candice Samples-Morris, Holly Simmons, Keri M. Ramsey, Meagan L. Whatley, Jane B. Lane

Open Access Commentary

Patient and Clinician Perspectives: To Create a Better Future for Chronic Kidney Disease, We Need to Talk About Our Kidneys

Pamela R. Kushner, Jane DeMeis, Petrina Stevens, Ana Marija Gjurovic, Elmas Malvolti, Navdeep Tangri

Open Access Review

Development of a Conceptual Model for the Patient Experience of Immunoglobulin A Nephropathy (IgAN): A Qualitative Literature Review

Natalie V. J. Aldhouse, Helen Kitchen, Tamara Al-Zubeidi, Madeleine Thursfield, Randall Winnette, Sandi See Tai, Linda Zhu, Cecilia Freitas, Nicolas Garnier, Christine L. Baker

Review

Evolving Role of Viltolarsen for Treatment of Duchenne Muscular Dystrophy

LeighAnn Y. Vincik, Alexandra D. Dautel, Abigail A. Staples, Lillian V. Lauck, Catherine J. Armstrong, Jeffery T. Howard, David McGregor, Shahab Ahmadzadeh, Sahar Shekoohi, Alan D. Kaye

Open Access Review

An Update on Stiripentol Mechanisms of Action: A Narrative Review

Alexandre Bacq, Antoine Depaulis, Vincent Castagné, Marie-Emmanuelle Le Guern, Elaine C. Wirrell, Marc Verleye

Original Research

Contraceptive Recommendations for Women with Immune-Mediated Inflammatory Diseases: A Delphi Consensus

José Manuel Carrascosa, Ana Echarri, Olga Gavín Sebastián, Paloma García de la Peña, Oscar Martínez Pérez, Susan Ramirez, Mónica Valderrama, María Montoro Álvarez

Open Access Original Research

Cost-Effectiveness Analysis of HRD Testing for Previously Treated Patients with Advanced Ovarian Cancer in Italy

Carla Rognoni, Domenica Lorusso, Francesco Costa, Patrizio Armeni

Original Research

Exploring Perceptions of Biologic Therapies: A Qualitative Study Among Canadians Living with Severe Asthma

Andrea Bever, Jessica Dunne, Jenna Reynolds, Susan Waserman, Alan G. Kaplan, Andrew O’Keefe, Stacey McNeilly, Shelagh M. Szabo

Open Access Original Research

Respiratory Syncytial Virus (RSV) Burden in Infants in the Kingdom of Saudi Arabia and the Impact of All-Infant RSV Protection: A Modeling Study

Adel Alharbi, Abdullah Yousef, Amal Zubani, Mohammad Alzahrani, Mohammad Al-Hindi, Saleh Alharbi, Turki Alahmadi, Hana Alabdulkarim, Paulina Kazmierska, Matthieu Beuvelet

Open Access Original Research

Exposure–Response Efficacy Modeling to Support Trofinetide Dosing in Individuals with Rett Syndrome

Mona Darwish, Julie Passarell, James M. Youakim, Heather Bradley, Kathie M. Bishop

Open Access Original Research

7-Year Efficacy and Safety of iStent inject Trabecular Micro-Bypass in Combined and Standalone Usage

Fritz H. Hengerer, Gerd U. Auffarth, Ina Conrad-Hengerer

Open Access Original Research

Assessing Itch Severity: Content Validity and Psychometric Properties of a Patient-Reported Pruritus Numeric Rating Scale in Atopic Dermatitis

Alissa Rams, Jessica Baldasaro, Laurine Bunod, Laure Delbecque, Sara Strzok, Juliette Meunier, Hany ElMaraghy, Luna Sun, Evangeline Pierce

Open Access Original Research

Risk Factors for Thromboembolic Events in Patients With Dialysis-Dependent CKD: Pooled Analysis of Phase 3 Roxadustat Trials in Japan

Takayuki Hamano, Yusuke Yamaguchi, Kashia Goto, Sho Mizokawa, Yuichiro Ito, Frank Dellanna, Jonathan Barratt, Tadao Akizawa

Open Access Original Research

Risk Factors for Thromboembolic Events in Patients With Dialysis-Dependent CKD: Pooled Analysis of Four Global Roxadustat Phase 3 Trials

Takayuki Hamano, Yusuke Yamaguchi, Kashia Goto, Shaka Martin, Alina Jiletcovici, Frank Dellanna, Tadao Akizawa, Jonathan Barratt

Open Access Original Research

Comparative Efficacy of Talquetamab vs. Current Treatments in the LocoMMotion and MoMMent Studies in Patients with Triple-Class-Exposed Relapsed/Refractory Multiple Myeloma

Hermann Einsele, Philippe Moreau, Nizar Bahlis, Manisha Bhutani, Laure Vincent, Lionel Karlin, Aurore Perrot, Hartmut Goldschmidt, Niels W. C. J. van de Donk, Enrique M. Ocio, Joaquin Martinez-Lopez, Paula Rodríguez-Otero, Dominik Dytfeld, Joris Diels, Vadim Strulev, Imene Haddad, Thomas Renaud, Eric Ammann, Jedelyn Cabrieto, Nolen Perualila, Ryan Gan, Youyi Zhang, Trilok Parekh, Claire Albrecht, Katja Weisel, Maria-Victoria Mateos

Original Research

Improved Quality of Life in Patients with Psoriasis Receiving Apremilast: Real-World Data from the Netherlands

Juul M. P. A. van den Reek, Robert J. T. van der Leest, Sarah E. Thomas, Ruud Prevoo, Margreet E. Plantenga, Elke M. G. J. de Jong

Open Access Original Research

Selective Internal Radiation Therapy Using Y-90 Resin Microspheres for Metastatic Colorectal Cancer: An Updated Systematic Review and Network Meta-Analysis

André L. F. Azeredo-da-Silva, Victor Hugo F. de Jesus, Ion Agirrezabal, Victoria K. Brennan, Phuong L. Carion, Nathalie Amoury, Bruna M. Vetromilla, Bruna S. Zanotto, Suki Shergill, Patricia K. Ziegelmann

Original Research

Identification of a Group of Therapeutic Targets and Prognostic Biomarker for Triple Negative Breast Cancer

Yan Li, Shengjie Yang, Lu Qi, Yinjuan Li, Xinghe Wang

Open Access Original Research

Projected Impact of Omidubicel-onlv on Racial/Ethnic Disparities in Allogeneic Hematopoietic Cell Transplantation (Allo-HCT) Outcomes in Hematologic Malignancies

Nandita Khera, Marie Louise Edwards, Yan Song, Rochelle Sun, Rocio Manghani, Heayoung Shin, Ronit Simantov, James Signorovitch, Smitha Sivaraman, Usama Gergis

Open Access Original Research

Treatment Patterns with Mirabegron and Antimuscarinics for Overactive Bladder: A Prospective, Registry Study in Taiwan and South Korea (FAITH)

Seung-June Oh, Sung Tae Cho, Hann-Chorng Kuo, Eric Chieh-Lung Chou, Yu-Chao Hsu, Kyu-Sung Lee, Farid Hadi, Yi Song, Budiwan Sumarsono

Open Access Original Research

Satisfaction with the Injection Experience of a New, Citrate-Free Formulation of Ixekizumab

Sanjay Chabra, Julie Birt, Rebecca Bolce, Jeffrey Lisse, William N. Malatestinic, Baojin Zhu, Miriam Kimel, Julie McCormack, Marissa Stefan, W. Chad Cragun

Original Research

Increased Nasal Blimp1 + Treg Cells After Sublingual Immunotherapy Reflect the Efficacy of Treatment in Allergic Rhinitis

Yue Pan, Xinxin Zhang, Huanting Geng, Yan Yu, Jianyong Liu, Menglin Li, Huijun Yang, Yifang Yuan, Yao Xu, Yujia Wu, Geping Wu, Xingkai Ma, Lei Cheng

Open Access Original Research

Incidence and Costs of Clinically Significant Events with Systemic Therapy in Patients with Unresectable Hepatocellular Carcinoma: A Retrospective Cohort Study

Daniel J. Simmons, Stephen J. Valerio, Darren S. Thomas, Marcus J. Healey, Zhuoxin Jiang, Jesica M. Levingston Mac Leod, Yian Lin, Janvi Sah

Open Access Original Research

Efficacy and Safety of Transitioning to Lemborexant from Z-drug, Suvorexant, and Ramelteon in Japanese Insomnia Patients: An Open-label, Multicenter Study

Motohiro Ozone, Susumu Hirota, Yu Ariyoshi, Kenichi Hayashida, Azusa Ikegami, Mitsunari Habukawa, Hayato Ohshima, Daisuke Harada, Hiroshi Hiejima, Nozomu Kotorii, Kenta Murotani, Takehiro Taninaga, Naohisa Uchimura

Open Access Correction

Correction to: Real-World Outcomes with Lomitapide Use in Paediatric Patients with Homozygous Familial Hypercholesterolaemia

Tawfeg Ben-Omran, Luis Masana, Genovefa Kolovou, Gema Ariceta, F. Javier Nóvoa, Allan M. Lund, Martin P. Bogsrud, María Araujo, Osamah Hussein, Daiana Ibarretxe, Rosa M. Sanchez-Hernández, Raul D. Santos

Correction

Correction to: Association of Patient Satisfaction with Cataract Grading in Five Types of Multifocal IOLs

Sana Niazi, Zisis Gatzioufas, Sorcha N. Dhubhghaill, Majid Moshirfar, Amir Faramarzi, Farzad Mohammadi, Bahar Kheiri, Alireza Peyman, Mohammad Heidari, Farideh Doroodgar

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