Ausgabe 4/2023
Inhalt (15 Artikel)
Real-world safety profile of eculizumab in patients with paroxysmal nocturnal hemoglobinuria, atypical hemolytic uremic syndrome, or generalized myasthenia gravis: an integrated analysis of post-marketing surveillance in Japan
Jun-ichi Nishimura, Tatsuya Kawaguchi, Shuichi Ito, Hiroyuki Murai, Akihiko Shimono, Takahisa Matsuda, Yuji Fukamizu, Hirozumi Akiyama, Hideo Hayashi, Takashi Nakano, Shoichi Maruyama
Lenalidomide treatment of Japanese patients with myelodysplastic syndromes with 5q deletion: a post-marketing surveillance study
Shuji Uno, Yoko Motegi, Kenichi Minehata, Yasuo Aoki
A retrospective analysis of clinical features and treatment outcome in 21 patients with immunoglobulin M-related light-chain amyloidosis in Japan: a study from the Amyloidosis Research Committee
Shin-ichi Fuchida, Mizuki Ogura, Tadao Ishida, Hiroyuki Hata, Hiroshi Handa, Nagaaki Katoh, Chiaki Nakaseko, Kazutaka Sunami, Yuta Katayama, Hironobu Nobata, Kazuiku Oshiro, Shinsuke Iida, Yoshiki Sekijima, Hironobu Naiki, Chihiro Shimazaki
Substitution of calcineurin inhibitors with corticosteroids after allogeneic hematopoietic cell transplantation
Shimpei Matsumi, Shun-ichi Kimura, Yuhei Nakamura, Masakatsu Kawamura, Junko Takeshita, Shunto Kawamura, Nozomu Yoshino, Yukiko Misaki, Kazuki Yoshimura, Ayumi Gomyo, Yosuke Okada, Yu Akahoshi, Masaharu Tamaki, Machiko Kusuda, Kazuaki Kameda, Hidenori Wada, Aki Tanihara, Miki Sato, Hideki Nakasone, Shinichi Kako, Yoshinobu Kanda
Antibody response after third dose of COVID-19 mRNA vaccination in allogeneic hematopoietic stem cell transplant recipients is comparable to that in healthy counterparts
Erina Takagi, Seitaro Terakura, Hidetsugu Fujigaki, Akinao Okamoto, Kotaro Miyao, Masashi Sawa, Takanobu Morishita, Tatsunori Goto, Yukiyasu Ozawa, Tetsuya Nishida, Nobuaki Fukushima, Kazutaka Ozeki, Ryo Hanajiri, Kuniaki Saito, Makoto Murata, Akihiro Tomita, Hitoshi Kiyoi
A case of cold agglutinin syndrome associated with chronic lymphocytic leukaemia harbouring mutations in CARD11 and KMT2D
Masahiko Fukatsu, Yoichi Hamazaki, Yuki Sato, Daisuke Koyama, Takayuki Ikezoe
New onset of hypomegakaryocytic thrombocytopenia with the potential for progression to aplastic anemia after BNT162b2 mRNA COVID-19 vaccination
Mirei Kobayashi, Akio Mori, Yoshitaka Oda, Emi Yokoyama, Minoru Kanaya, Koh Izumiyama, Makoto Saito, Shinya Tanaka, Masanobu Morioka, Takeshi Kondo
Venetoclax with CAG regimen for early T-cell precursor acute lymphoblastic leukemia: a case report and literature review
Yihan Zhao, Shiqing Jiang, Yujun Tang, Lin Zhao
Mutated ZRSR2 and CUL3 accelerate clonal evolution and confer venetoclax resistance via RAS signaling pathway in blastic plasmacytoid dendritic cell neoplasm
Koichiro Fukuchi, Daisuke Koyama, Maki Takada, Hirotaka Mori, Kiyohito Hayashi, Naomi Asano, Yuki Sato, Masahiko Fukatsu, Motoki Takano, Hiroshi Takahashi, Kayo Shirado-Harada, Satoshi Kimura, Toshiyuki Yamamoto, Takayuki Ikezoe
Clinical and genetic features of Japanese cases of MDS associated with VEXAS syndrome
Hiroyoshi Kunimoto, Ayaka Miura, Ayaka Maeda, Naomi Tsuchida, Yuri Uchiyama, Yosuke Kunishita, Yuki Nakajima, Kaoru Takase-Minegishi, Ryusuke Yoshimi, Takuya Miyazaki, Maki Hagihara, Etsuko Yamazaki, Yohei Kirino, Naomichi Matsumoto, Hideaki Nakajima
Newly diagnosed extranodal NK/T-cell lymphoma, nasal type, at the injected left arm after BNT162b2 mRNA COVID-19 vaccination
Takuto Tachita, Takenori Takahata, Satoru Yamashita, Toru Ebina, Kosuke Kamata, Kazufumi Yamagata, Yoshiko Tamai, Hirotake Sakuraba
Transcriptome sequencing identifies novel EVX fusions involved in transcriptional activation of HOX family genes in pediatric immature T-cell acute lymphoblastic leukemia: two cases reports and a literature review
Xiao Zhang, Bowen Cui, Yizhen Li, Zhiheng Li, Jiajia Zheng, Xinran Chu, Peifang Xiao, Jun Lu, Zheng Wang, Jiannong Cen, Yu Liu, Shaoyan Hu
Acute monocytic leukemia with KMT2A::LASP1 developed 9 months after diagnosis of acute megakaryoblastic leukemia in a 2-year-old boy
Takashi Fujita, Hiroko Fukushima, Toru Nanmoku, Yuki Arakawa, Takao Deguchi, Ryoko Suzuki, Yuni Yamaki, Sho Hosaka, Hidetoshi Takada
Successful treatment of DOCK8 deficiency by allogeneic hematopoietic cell transplantation from alternative donors
Asuka Kono, Manabu Wakamatsu, Yoshihiro Umezawa, Hideki Muramatsu, Hiroki Fujiwara, Dan Tomomasa, Kento Inoue, Keiichiro Hattori, Tetsuo Mitsui, Hidetoshi Takada, Yoshiyuki Minegishi, Yoshiyuki Takahashi, Masahide Yamamoto, Takehiko Mori, Hirokazu Kanegane
Measurable residual disease in Japanese patients with relapsed or refractory chronic lymphocytic leukemia treated with venetoclax
Koji Izutsu, Kazuhito Yamamoto, Koji Kato, Takayuki Ishikawa, Noriko Fukuhara, Yasuhito Terui, Ilseung Choi, Sumiko Okubo, Natsumi Ogawa, Mizu Sakai, Yasuko Nishimura, Brenda Chyla, Yan Sun, Dai Maruyama